|
ABEO
|
Abeona Therapeutics Inc.
|
US
|
NASDAQ
|
|
ACER
|
Acer Therapeutics Inc.
|
US
|
NASDAQ
|
|
AKTX
|
Akari Therapeutics Plc
|
US
|
NASDAQ
|
|
ALDX
|
Aldeyra Therapeutics, Inc.
|
US
|
NASDAQ
|
|
AURA
|
Aura Biosciences, Inc.
|
US
|
NASDAQ
|
|
AVRO
|
AVROBIO, Inc.
|
US
|
NASDAQ
|
|
BLUE
|
bluebird bio, Inc.
|
US
|
NASDAQ
|
|
BMRN
|
BioMarin Pharmaceutical Inc.
|
US
|
NASDAQ
|
|
CNTG
|
Centogene N.V.
|
US
|
NASDAQ
|
|
CYTH
|
Cyclo Therapeutics, Inc.
|
US
|
NASDAQ
|
|
DSGN
|
Design Therapeutics, Inc.
|
US
|
NASDAQ
|
|
ELOX
|
Eloxx Pharmaceuticals, Inc.
|
US
|
NASDAQ
|
|
FIXX
|
Homology Medicines, Inc.
|
US
|
NASDAQ
|
|
FOLD
|
Amicus Therapeutics, Inc.
|
US
|
NASDAQ
|
|
GBIO
|
Generation Bio Co.
|
US
|
NASDAQ
|
|
GSK
|
GlaxoSmithKline PLC
|
US
|
NYSE
|
|
INM
|
InMed Pharmaceuticals Inc.
|
US
|
NASDAQ
|
|
IONS
|
Ionis Pharmaceuticals, Inc.
|
US
|
NASDAQ
|
|
KROS
|
Keros Therapeutics, Inc.
|
US
|
NASDAQ
|
|
KRYS
|
Krystal Biotech, Inc.
|
US
|
NASDAQ
|